Idursulfase:A Magic Potion To Rewrite The Treatment Pattern Of Mucopolysaccharidosis Type II
Idursulfase, also known as Elaprase, is used for enzyme replacement therapy in patients diagnosed with mucopolysaccharidosis type II (MPS II, Hunter syndrome).
Mucopolysaccharidosis Type II: A Rare And Complex Disease
Mucopolysaccharidosis Type II is an X-chromosome linked lysosomal storage disease, in which patients are unable to properly break down certain glycosaminoglycans (GAGs) due to a lack of iduronase in the body, resulting in the accumulation of these substances in the body.
The symptoms of the disease include delayed growth and development, skeletal deformities, joint stiffness, intellectual disability, and respiratory problems.
At present, the main treatment for Hunter syndrome is enzyme replacement therapy (ERT), but its effectiveness is limited and it requires frequent intravenous infusion, which imposes a huge burden on patients and families.
Idursulfase: A Key Drug For Treating Mucopolysaccharidosis Type II
Elaprase Idursulfase is an enzyme replacement therapy used to treat Hunter syndrome (mucopolysaccharidosis type II, MPS II).
Mucopolysaccharidosis Type II is a rare genetic disorder caused by a lack of iduronic acid-2-sulfatase in China, which results in specific byproducts on systemic scaffolds, leading to symptoms such as walking and breathing difficulties.
Future Prospects
With the continuous advancement of science and technology, innovative therapies for idurase deficiency are gradually moving from the laboratory to clinical practice.
The success of gene therapy may not only change the lives of patients with Mucopolysaccharidosis Type II, but also provide important insights for the treatment of other inherited lysosomal storage diseases.
In the future, we look forward to more research and collaboration to bring more hope and choices to rare disease patients.
However, DengYue‘s efforts to increase the affordability of the medicine are critical to ensuring that more patients benefit from it. So please feel free to inquiry us for Elaprase.
Information from DengYue Medicine, HongKong Drug Wholesale Distributor offers this information as a guide, not a substitute for professional medical advice. Consult your doctor before any treatment.
